Scientific Directory

Dr Cécile GASTALDI
Ingénieur de Recherche - Équipe Biothérapies Appliquées aux Handicaps Neuromusculaires (LIA-BAHN)Tel. +377 97 77 44 41
Email : [javascript protected email address]
Thèmes de recherche développés
Publications CSM
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A group of novel VEGF splice variants as alternative therapeutic targets in renal cell carcinoma
Montemagno C, Durivault J, Gastaldi C, Dufies M, Vial V, He X, Ambrosetti D, Kamenskaya A, Négrier S, Bernhard J-C, Borchiellini D, Cao Y, Pagès G
mol 21 Feb 2023, 45 -
Palmitic acid conjugation enhances potency of tricyclo-DNA splice switching oligonucleotides
Relizani K, Echevarria L, Zarrouki F, Gastaldi C, Dambrune C, Aupy P, Haeberli A, Komisarski M, Tensorer T, Larcher T, Svinartchouk F, Vaillend C, Garcia L, Goyenvalle A
nar Vol. 50, No. 1, 17–34 -
Long-Term Efficacy of AAV9-U7snRNA-Mediated Exon 51 Skipping in mdx52 Mice
Aupy P, Zarrouki F, Sandro Q, Gastaldi C, Buclez P-O, Mamchaoui K, Garcia L, Vaillend C, Goyenvalle A
Molecular Therapy: Methods & Clinical Development 17: 1037-1047